Haydar Frangoul – CRISPR-Cas9 Gene Editing for Sickle Cell Disease and Transfusion Dependent β-Thalassemia | GES Colloquium
Haydar Frangoul – CRISPR-Cas9 Gene Editing for Sickle Cell Disease and Transfusion Dependent β-Thalassemia | GES Colloquium
A presentation of data on using gene addition and gene editing technology to treat patients with sickle cell disease and transfusion dependent beta thalassemia.